Ocugen, Inc. gene therapy outlook: key 2026 catalysts, Phase 2/3 eye-disease data, BLA plans to 2028, and risks. Click for ...

A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

Gene therapy treatments for rare diseases are being developed, but getting them out of the lab has proved challenging.

People looking to lose weight and lower their blood sugar may someday be able to get a single injection that turns their cells into tiny factories churning out a protein that is essentially the active ...

The new method is designed to focus specifically on pain-related signals, without interfering with normal activity in other parts of the brain. A new preclinical study has identified a gene therapy ap ...

A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of ...

Osaka, Japan - A research team at The University of Osaka has unveiled the molecular mechanism behind genome ejection from adeno-associated virus (AAV) vectors, a crucial delivery vehicle in gene ...

Scientists from the Centenary Institute and the University of Sydney have made a landmark discovery that could lead to safer and more effective gene therapies for a range of serious genetic disorders ...

Cell and gene therapies use the body's building blocks - cells and genetic material - to boost the immune system or correct ...